The mum of eleven month old Edward says “he has been given a future” after receiving gene-therapy for Spinal Muscular Atrophy. Baby Edward came to Sheffield Children’s to receive the potentially life-saving drug Zolgensma, which can prevent paralysis and...
A two month old baby is the first patient in Yorkshire to receive a potentially life-saving drug that can prevent paralysis and prolong the lives of children with Spinal Muscular Atrophy (SMA). Baby Markuss received the drug Zolgensma, which...
Meet five year old Elijah, he lives in Leicestershire and travels up to Sheffield Children’s every 16 weeks for treatment. In 2019, Elijah was diagnosed with Spinal Muscular Atrophy (SMA) Type 2 after a genetics investigation, following an earlier...
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